• STAT+: The price of a Vertex cystic fibrosis treatment stirs anger in Australia

    12 days ago - By STAT

    The latest dustup over the cost of cystic fibrosis medicines sold by Vertex Pharmaceuticals is taking place in Australia, where an independent committee recommended that the government not cover a new combination treatment due to the cost and financial implications.
    In explaining its decision, the Pharmaceutical Benefits Advisory Committee acknowledged that the medicine, called Trikafta, provided a significant benefit for some patients, especially those with a particular gene mutation. But the PBAC also noted that the cost effectiveness had not been satisfactorily established and deferred...
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