• STAT+: Sarepta's more potent Duchenne treatment shows promise, greater toxicity, in small study

    4 days ago - By STAT

    Sarepta Therapeutics said Monday that a second-generation medicine for patients with a certain type of Duchenne muscular dystrophy showed improved performance in laboratory tests over the biotech's marketed treatment.
    In a small clinical trial, a monthly infusion of the new Sarepta drug, called SRP-5051, produced eight times more of the muscle protein dystrophin compared to weekly infusions of Exondys 51, the company's existing product. Continue to STAT+ to read the full story...
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