• STAT+: FDA approves a gene therapy for the inherited bleeding disorder hemophilia B

    10 days ago - By STAT

    The Food and Drug Administration on Tuesday approved the first gene therapy to treat people with hemophilia B, an inherited bleeding disorder.
    The one-time treatment, called Hemgenix, was developed by the Dutch biotech company UniQure and will be marketed by CSL Behring, an Australian pharmaceutical company. Continue to STAT+ to read the full story...
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